Capricor CEO to Present at American Society of Gene and Cell Therapy Annual Meeting Ahead of Q1 Earnings Update
May 13 is a busy day for biotechnology company Capricor Therapeutics (NASDAQ: CAPR). The company which focuses on…
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Gene and Cell Therapy
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When you think of the future, keep in mind that the field of regenerative medicine is rapidly advancing. Cell and gene therapies are a new kind of medicine with enormous potential still to be realized. Most current, small-molecule medicines are made in a standardized way and have a limited lifespan within the body.
Cell and gene therapies are not the same as existing drugs. They entail removing cells, protein, or genetic material (DNA) from the patient (or a donor), modifying them in a personalized way for individual needs before re-injecting them into the patient.
Cell and gene therapies may provide longer-lasting effects than traditional medicines. They have the potential to treat serious illnesses such as motor neuron disease, as well as a variety of uncommon problems for which there are no effective treatments.
Gene Therapy
Gene therapy in its most broad definition is the use of genetic material to cure or treat a disease. The introduced genetic material affects how a single protein or group of proteins is manufactured by the cell.
A variety of diseases have been treated with gene therapy, including muscular dystrophy and Leber’s congenital amaurosis. It can be used to decrease levels of a disease-causing form of a protein, increase production of disease-fighting proteins, or generate new/modified proteins.
Cell Therapy
Cell therapy is the transfer of viable, live cells into a patient to assist with curing or treating an illness. The cells may come from the patient (autologous) or a donor (allogeneic). Cells used in cell therapy can be categorized according to their potential to convert into various cell types. The type of cells administered to the patient depends on the treatment needs.
Cell Therapy vs. Gene Therapy
Cell therapy is a treatment that aims to cure illnesses by regenerating or modifying specific sets of cells, as well as using cells to deliver a drug via circulation throughout the body.
The cells may be fabricated outside the body and then injected into the patient with cell therapy. Autologous cells come from the patient (end autologous), whereas allogeneic cells do not (end allogeneic).
Gene therapy seeks to cure diseases by replacing, inactivating, or introducing genes into cells inside or outside the body (in vivo) or vice versa (ex vivo).
Both cell and gene therapies are referred to as “treatments.” These treatments function by modifying genes in particular sorts of cells and transplanting them into the body. Some therapies are considered both cell and gene therapies.